New Pharmacological Approaches to Treat Patients with Cystic Fibrosis with Nonsense Mutations

Am J Respir Crit Care Med. 2016 Nov 1;194(9):1042-1044. doi: 10.1164/rccm.201605-1021ED.
No abstract available

Publication types

  • Comment

MeSH terms

  • Codon, Nonsense*
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics
  • Cystic Fibrosis*
  • Humans
  • Mutation

Substances

  • Codon, Nonsense
  • Cystic Fibrosis Transmembrane Conductance Regulator